As gene therapy for Duchenne muscular dystrophy faces scrutiny after tragic deaths, families like the Revells navigate the uncertain waters of hope and risk, questioning the future of their loved ones.
In a stunning move, the FDA has put clinical trials for Sarepta's gene therapy on hold due to alarming safety concerns after multiple patient deaths linked to acute liver failure. The company faces scrutiny as it navigates the fallout.
Sarepta Therapeutics is under fire as another patient succumbs to acute liver failure linked to its gene therapy trial for muscular dystrophy, adding to the recent deaths of two teenage boys.
Isomorphic Labs, leveraging AI breakthroughs from DeepMind, is on the brink of human clinical trials for cancer drugs. With major pharma partnerships, the future of drug design looks promising!
A groundbreaking study reveals that a blood test can identify Alzheimer's patients at risk of rapid decline. Researchers highlight the importance of insulin resistance in accelerating cognitive impairment, opening doors for timely interventions.
In a bold move, over 90 NIH scientists have signed the Bethesda Declaration, challenging their new leader Jay Bhattacharya and the Trump administration's policies that threaten public health research and safety.
In a surprising move, the HHS has terminated a $590 million contract with Moderna for H5 avian influenza vaccine development, raising alarms among health experts amidst rising H5N1 threats.
The FDA has approved Lumipulse, the first blood test for diagnosing Alzheimer’s, offering a simpler and less invasive option compared to traditional methods like PET scans. Experts believe this could revolutionize care and research.
Recent clinical trials show that GLP-1 weight loss medications like Zepbound are more effective for women than men, prompting researchers to explore the biological and societal reasons behind this phenomenon.
A new NIH-funded study reveals crucial protein changes in spinal fluid that may provide the first specific biomarkers for frontotemporal dementia (FTD), paving the way for earlier diagnosis and treatment options.
